For the first time, doctors have used gene therapy to stave off a fatal degenerative brain disease, an achievement that some experts had thought impossible. The key to making the therapy work? One of medicine’s greatest villains: HIV. The patients were children who had inherited a mutated gene causing a rare disorder, adrenoleukodystrophy, or ALD. Nerve cells in the brain die, and in a few short years, children lose the ability to walk or talk. They become unable to eat without a feeding tube, to see, hear or think. They usually die within five years of ...
In a first, gene therapy halts a fatal brain disease
The key to making the therapy work? One of medicine's greatest villains: HIV
Gina Kolata | NYT Last Updated at October 7, 2017 22:22 IST